Pipeline

Disease Area Indication Target factor Seed Pre-Clinical Phase I
Local tissue regeneration
Osteo arthritis
mRNA: RUNX1
Partner: Axcelead Inc.
Skin
mRNA: F
Ophthalmic
mRNA: C
Partner: Not disclosed
Vaccine
Allergy
mRNA: B
Partner: Kao Corporate
Infection
mRNA: A
Partner: Crafton Biotechnology / MAB
Allergy
mRNA: G
Partner: Kao Corporate
Autoimmune disease
mRNA: H
Partner: Kao Corporate
Oncology
GBM
ASO: TUG1
Partner: Nagoya University
HER2-negative
breast cancer
siRNA: PRDM14
Partner: Keio University