Pipeline

Disease Area Indication Target factor Seed Pre-Clinical Phase I
Local tissue regeneration
Osteo arthritis
mRNA: RUNX1
Partner: Axcelead Inc.
Skin
mRNA: F
Ocular
mRNA: C
Otolaryngological
mRNA: D
Vaccine
Immune
mRNA: B
Partner: Kao Corporate
Infection
mRNA: A
Partner: Crafton Biotechnology / MAB
Oncology
mRNA: E
Oncology
GBM
ASO: TUG1
Partner: NAGOYA University
HER2-negative
breast cancer
siRNA: PRDM14
Partner: Keio University